Bleeding Disorders Overview
🧬 Haemophilia A
- Deficiency: Factor VIII (FVIII)
- Inheritance: X-linked recessive
- Incidence: ~1 in 5,000 male births
- Most common severe inherited coagulation disorder
- Females are carriers; rarely symptomatic unless lyonisation skewed
- Carrier females may have low FVIII levels — screen them
APTT prolonged
PT normal
TT normal
🧬 Haemophilia B (Christmas Disease)
- Deficiency: Factor IX (FIX)
- Inheritance: X-linked recessive
- Incidence: ~1 in 30,000 male births
- Clinically identical to Haemophilia A — distinguished by factor assay
- Named after Stephen Christmas, first diagnosed patient (1952)
APTT prolonged
PT normal
TT normal
Severity Classification
SEVERE
- Spontaneous joint/muscle bleeds
- Haemarthrosis from childhood
- Requires prophylaxis
MODERATE
- Bleeds with mild trauma
- Occasional spontaneous bleeds
- May not need prophylaxis
MILD
- Bleeds with significant trauma/surgery
- May be undiagnosed for years
- DDAVP may be adequate
Clinical Features
🦴 Haemarthrosis (Joint Bleeds)
- Most common: knees, elbows, ankles
- Warmth, swelling, pain, reduced range of motion
- Repeated bleeds → chronic haemophilic arthropathy
- Target joint: same joint bled 3+ times in 6 months
- Synovitis → cartilage destruction → disability
💪 Muscle Bleeds
- Iliopsoas bleed: hip flexion pain, groin/back pain, femoral nerve palsy
- Compartment syndrome risk with forearm/calf bleeds
- Monitor neurovascular status (pulses, sensation, movement)
- CT/ultrasound to assess extent
🧠 Intracranial Bleeding
EMERGENCY: Any headache, confusion, vomiting, neurological deficit — treat IMMEDIATELY with factor to 100% before imaging if delay anticipated.
- Most dangerous complication — 30% of haemophilia deaths
- Can be spontaneous in severe disease
- Symptoms: severe headache, drowsiness, fitting, focal signs
- CT head + neurosurgical referral + haematology input
🩸 Other Bleeding Sites
- Mucosal: epistaxis, gum bleeding, haematuria
- GI bleeding: haematemesis, melaena
- Soft tissue haematomas
- Delayed surgical bleeding (hours/days post-op)
- Neonatal: intracranial bleed at delivery, cephalhaematoma, circumcision bleed
von Willebrand Disease (vWD)
Most common hereditary bleeding disorder — affects ~1% of population. Both males and females equally affected.
Type 1
- Partial quantitative deficiency of vWF
- Autosomal dominant
- Commonest type (75%)
- Responds well to DDAVP
- Mild mucocutaneous bleeding
Type 2
- Qualitative defect in vWF (A/B/M/N subtypes)
- Autosomal dominant mostly
- DDAVP contraindicated in type 2B (thrombocytopenia worsening)
- Requires vWF concentrate
Type 3
- Complete absence of vWF
- Autosomal recessive
- Severe — resembles haemophilia A
- DDAVP ineffective
- vWF/FVIII concentrate required
Platelet Disorders
🔵 ITP — Immune Thrombocytopenic Purpura
- Autoimmune destruction of platelets
- Platelet count <100 × 10⁹/L
- Petechiae, purpura, bruising, mucosal bleeding
- Treatment: corticosteroids, IVIG, TPO agonists, rituximab, splenectomy
🔵 Hereditary Platelet Disorders
- Glanzmann's thrombasthenia: absent GPIIb/IIIa — platelet aggregation failure — autosomal recessive — platelet transfusion/rFVIIa
- Bernard-Soulier syndrome: absent GPIb — platelet adhesion failure — large platelets — autosomal recessive
Coagulation Screen Interpretation
| Condition | PT | APTT | TT | Fibrinogen | Platelets |
| Haemophilia A/B | Normal | Prolonged ↑ | Normal | Normal | Normal |
| vWD (most types) | Normal | +/- Prolonged | Normal | Normal | Normal |
| Warfarin / Vit K deficiency | Prolonged ↑ | +/- Prolonged | Normal | Normal | Normal |
| DIC | Prolonged ↑ | Prolonged ↑ | Prolonged ↑ | Low ↓ | Low ↓ |
| ITP | Normal | Normal | Normal | Normal | Low ↓ |
| Heparin therapy | Normal | Prolonged ↑ | Prolonged ↑ | Normal | Normal |
| Glanzmann's/BSS | Normal | Normal | Normal | Normal | Normal count |
Key nursing point: A prolonged APTT with normal PT in a male patient = haemophilia A or B until proven otherwise. Always send mixing studies (1:1 normal plasma) — correction = factor deficiency; no correction = inhibitor.
Factor Replacement Therapy
💉 Factor VIII Concentrates
Haemophilia A
- Plasma-derived: Octanate, Haemate P (contains vWF — useful for vWD)
- Recombinant (preferred): Advate, Kogenate FS, Nuwiq, Kovaltry
- Recombinant preferred — no blood-borne infection risk
- Standard half-life: 8–12 hours → dosing 2–3x/week
- Store at 2–8°C or room temperature per product instructions
💉 Factor IX Concentrates
Haemophilia B
- Plasma-derived: Mononine, Immunine
- Recombinant (preferred): BeneFIX, Rixubis, Idelvion
- Half-life 18–24 hours → less frequent dosing
- Volume of distribution larger than FVIII — dosing formula differs
Dosing Formulae
Haemophilia A: Dose (IU) = Weight (kg) × Desired Rise (%) × 0.5
Haemophilia B: Dose (IU) = Weight (kg) × Desired Rise (%) × 1.0
Example — Haemophilia A
Patient weight70 kg
Desired FVIII rise50% (moderate bleed)
Dose70 × 50 × 0.5 = 1,750 IU
Repeat dose in8–12 hours
Example — Haemophilia B
Patient weight70 kg
Desired FIX rise50% (moderate bleed)
Dose70 × 50 × 1.0 = 3,500 IU
Repeat dose in18–24 hours
Target Factor Levels by Clinical Situation
| Clinical Situation | Target Factor Level | Duration | Frequency |
| Minor bleed (haemarthrosis, small muscle) | 30–50% | 1–3 days | Once or twice |
| Moderate bleed (major muscle, mouth, tongue) | 50–80% | 3–5 days | Every 8–24h |
| Life/limb-threatening bleed (ICH, neck, iliopsoas) | 80–100% | 7–14 days | Every 8–12h (FVIII) |
| Major surgery (pre-operative) | 100% | Until healing | Continuous infusion or bolus q8h |
| Minor surgery / dental extraction | 50% | 1–3 days | Single dose + tranexamic acid |
| Prophylaxis (severe haemophilia) | >1% trough | Lifelong | 3x/week or EOD |
Half-Lives & Extended Half-Life (EHL) Products
⏱️ Standard Half-Lives
Factor VIII8–12 hours
Factor IX18–24 hours
Repeat dose neededFVIII q8–12h; FIX q24h
Higher peak, shorter duration — requires frequent IV access
⏱️ Extended Half-Life (EHL) Products
- EHL FVIII: Elocta (rFVIIIFc) — half-life ~19h, twice weekly
- EHL FIX: Alprolix (rFIXFc) / Idelvion — half-life up to 102h, once weekly or fortnightly
- Major benefit for GCC patients: fewer infusions, better adherence
- Reduced burden for families with multiple affected children
- Especially valuable in Ramadan — fewer daily infusions
Inhibitor Development
Inhibitors are neutralising IgG antibodies against infused factor — the most serious treatment complication of haemophilia.
- 15–30% of severe haemophilia A develop inhibitors
- 1–5% of haemophilia B develop inhibitors
- High titre: >5 Bethesda Units (BU) — standard factor ineffective
- Low titre: <5 BU — high-dose factor may still work
- Bethesda assay / Nijmegen modification used for measurement
Bypassing Agents for Inhibitor Patients
rFVIIa (NovoSeven)90–120 mcg/kg IV q2–3h
aPCC (FEIBA)50–100 IU/kg q8–12h (max 200 IU/kg/day)
Caution: Never combine rFVIIa and aPCC — risk of thrombosis/DIC.
Factor Administration — Nursing Technique
1
ReconstitutionWarm vials to room temperature. Use provided diluent. Gently rotate — do NOT shake (denaturation risk). Inspect for particulates.
2
IV AdministrationPeripheral IV or implanted port (PAC/portacath). Slow IV push — typical rate 2–3 mL/min (FVIII). Check product PI for FIX rate limits.
3
Post-InfusionDocument: lot number, expiry, dose given, time, site. Flush with normal saline. Observe 20 min for allergic reaction.
4
MonitoringPost-infusion factor level at 15 min (peak) and 1h (in vivo recovery). Monitor bleed response. Report inadequate response immediately — suspect inhibitor.
Non-Factor Treatments & Prophylaxis
💊 Emicizumab (Hemlibra) — Game Changer
Bispecific antibody that bridges FIXa and FX, mimicking FVIII function — subcutaneous injection. Licensed for Haemophilia A with AND without inhibitors.
MechanismBridges FIXa + FX (FVIII bypass)
RouteSubcutaneous injection
Dosing optionsWeekly / Fortnightly / Monthly
Loading dose3 mg/kg SC weekly × 4 weeks
Maintenance1.5 mg/kg weekly (or 3 mg/kg 2-weekly)
Half-life~4–5 weeks
Nursing Considerations
- Teach SC injection technique — patient/carer self-administration
- Rotate injection sites: abdomen / thigh / upper arm
- TMA (thrombotic microangiopathy) risk if aPCC used concurrently — avoid aPCC >100 IU/kg/day total >24h
- Monitor for TMA: haematuria, thrombocytopenia, rising creatinine
- APTT is artificially shortened on emicizumab — do NOT use APTT to monitor
- GCC benefit: monthly dosing option ideal for Ramadan/Hajj
Desmopressin (DDAVP)
For mild Haemophilia A & vWD Type 1
MechanismReleases stored FVIII & vWF from endothelium
IV/SC dose0.3 mcg/kg in 50 mL NS over 30 min
IntranasalStimate: 150 mcg (<50kg) / 300 mcg (≥50kg)
Response monitoringFVIII level at 1h post-dose
TachyphylaxisAfter 3 doses — storages depleted
Hyponatraemia risk: DDAVP causes water retention (ADH effect). Fluid restrict to 1L/24h post-dose. Monitor serum sodium — especially in children, elderly, cardiac patients.
Contraindications
- vWD type 2B (worsens thrombocytopenia)
- Haemophilia B (no FVIII stores to release)
- Severe haemophilia A (insufficient stores)
- Cardiovascular disease (vasoactive effects)
- Children under 2 years
Tranexamic Acid
Antifibrinolytic agent — prevents clot breakdown. Excellent for mucosal and surface bleeding.
MechanismInhibits plasminogen activators → prevents fibrinolysis
Oral dose15–25 mg/kg TDS (adults: 1g TDS)
IV dose10 mg/kg TDS
Mouthwash10 mL of 5% solution QDS × 5–7 days (dental)
Best forDental, mucosal, epistaxis, menorrhagia
NEVER use tranexamic acid in haematuria — risk of obstructive clot formation in the ureter leading to renal colic and urinary obstruction. Ensure adequate hydration and use factor only for haematuria.
- Available in GCC formularies — widely accessible
- Halal-compliant — no animal-derived components
- Often combined with DDAVP or factor therapy
Primary Prophylaxis — Prevention of Joint Disease
Gold standard for severe haemophilia A & B: Start factor prophylaxis before first joint bleed, ideally by age 2–3 years (joint-protective). Goal: trough factor level >1%.
Standard prophylaxis (Haem A)25–40 IU/kg 3x/week or EOD
Standard prophylaxis (Haem B)40–60 IU/kg 2x/week
EHL FVIII prophylaxis50 IU/kg twice weekly
EHL FIX prophylaxis40–75 IU/kg once weekly
Emicizumab prophylaxis1.5 mg/kg weekly SC
Nursing Role in Prophylaxis
- Educate family on importance of compliance
- Teach home infusion technique (3–5 years of age)
- Monitor joint health: annual joint score (Pettersson score/Haemophilia Joint Health Score)
- Arrange physiotherapy for joint rehabilitation
- Breakthrough bleeds on prophylaxis = inhibitor screen
Fitusiran & Concizumab (Emerging Therapies)
Fitusiran (Alhemo)
- siRNA — silences antithrombin synthesis
- Monthly SC injection
- For Haemophilia A & B with/without inhibitors
- Risk of thrombosis — strict monitoring required
Concizumab (Alhemo)
- Anti-TFPI antibody — blocks tissue factor pathway inhibitor
- Daily SC injection
- Works for Haemophilia A, B and inhibitor patients
- Expanding formulary options in GCC
Acute Bleed Management
Core Principle: Treat within 2 hours of bleed onset — early treatment prevents progression, reduces factor required, preserves joint function.
🧊 RICE Principle + PROMPT Factor Treatment
RestImmobilise affected joint/limb immediately
IceIce pack (wrapped in cloth) 15–20 min — reduces swelling
CompressionElastic bandage — not too tight
ElevationElevate limb above heart level
PROMPT factor therapy is paramount. RICE alone is insufficient. Administer appropriate factor within 2 hours of bleed onset. Do not delay for investigations.
- NSAIDs/Aspirin/Ibuprofen — STRICTLY contraindicated (platelet inhibition)
- Paracetamol/Codeine for analgesia
- COX-2 inhibitors (celecoxib) — safer alternative in chronic arthropathy
Specific Bleed Sites
🦴 Haemarthrosis (Joint Bleed)
- Most common: knee (45%) → elbow (30%) → ankle (15%)
- Signs: warmth, swelling, stiffness, flexion posture, painful ROM
- Give factor immediately (target 30–50% for acute bleed)
- Rest in position of comfort (slight flexion for knee)
- Aspiration: do NOT aspirate in community — hospital only, under factor cover
- Physiotherapy after resolution — range of motion exercises
- Repeated bleeds in same joint = target joint — escalate to haematologist
💪 Muscle Bleeds
- Iliopsoas bleed: groin/hip/back pain, hip held in flexion, femoral nerve stretch sign positive
- Femoral nerve palsy risk: numbness anterior thigh, quadriceps weakness
- Target: 80% factor — admit for monitoring
- CT/MRI to confirm and quantify
- Compartment syndrome risk: calf, forearm bleeds — hourly neurovascular obs
- Monitor: distal pulses, cap refill, sensation, power (6Ps)
🧠 Intracranial Haemorrhage (ICH) — EMERGENCY
LIFE-THREATENING EMERGENCY. Any head injury or new headache in a person with haemophilia = treat FIRST, investigate second.
Warning Symptoms
- Sudden severe headache ("worst headache of life")
- Vomiting, drowsiness, confusion
- Seizures
- Focal neurological deficits
- Neck stiffness
Immediate Management
- Administer factor concentrate IMMEDIATELY — target 100%
- Call senior haematologist
- Urgent CT head (after factor given if delay <15 min)
- Neurosurgical referral if haematoma
- ICU involvement for monitoring
- Continue factor for minimum 14 days
🦷 Dental Procedures
- Pre-procedure: DDAVP (mild HemA/vWD1) OR factor to 50%
- Tranexamic acid mouthwash 10 mL QDS for 5–7 days post-extraction
- Tranexamic acid oral 1g TDS × 5 days
- Topical thrombin/fibrin sealant at socket
- Coordinate with haemophilia nurse specialist pre-procedure
- Nerve block injections require factor cover — haematoma risk
- Regular dental hygiene essential — prevent need for procedures
💋 Mucosal & Other Bleeds
- Epistaxis: first aid pressure 20 min; tranexamic acid oral; nasal cautery under factor cover if persistent
- Gum bleeding: tranexamic acid mouthwash; local pressure; dental referral
- GI bleed: factor replacement + GI endoscopy under cover; tranexamic acid IV
- Haematuria: hydration 3L/24h; factor if severe; NO tranexamic acid
- Menorrhagia: tranexamic acid + hormonal therapy; consider vWD/carrier state
Trauma Assessment Protocol
1
Treat first — alwaysAdminister factor at 100% immediately for any significant trauma. Do not wait for imaging results.
2
ABCDE assessmentStandard trauma assessment alongside haemostatic management. Secure IV access. Cross-match blood.
3
ImagingCT head for any head injury, even minor. Ultrasound/MRI for soft tissue and muscle bleeds. X-ray for joint assessment.
4
Haematology notificationAlert on-call haematologist for any significant trauma. Inhibitor screen if poor response to initial factor dose.
Medications to AVOID: Aspirin, NSAIDs, IM injections (use SC/IV routes only), arterial punctures without prolonged pressure, rectal temperature/procedures (risk of bleeding).
Comprehensive Care Centre & Home Treatment
🏥 Haemophilia Nurse Specialist Role
- Lead factor education sessions for patients and families
- Home therapy programme training and certification
- Prophylaxis monitoring and dose optimisation
- Inhibitor surveillance — annual Bethesda assay
- Joint assessment using validated scoring tools
- Maintain haemophilia registry and treatment records
- Coordinate multidisciplinary care: haematologist/physiotherapist/orthopaedic/dentist
- Emergency planning and patient safety netting
- School liaison for children with haemophilia
- Psychological support for chronic disease burden
- Travel and Hajj preparation advice
- Research and clinical trial support
Home Therapy Programme
1
Assessment for suitabilityPatient/carer motivation, visual acuity, manual dexterity, home storage facilities (fridge), sharps disposal access.
2
Vein access trainingPeripheral venepuncture technique. Vein preservation strategies. Central venous access device (portacath) insertion for small/difficult veins — common in young children.
3
Reconstitution and administrationAseptic technique. Product-specific reconstitution. Administration rate. Sharps safety — never recap needles. Sharps disposal containers.
4
Documentation and stock managementBleed diary/app (e.g., HaemoAssist). Treatment log: date/time/reason/dose/lot number. Cold chain management. Supply ordering and emergency stock.
5
Competency sign-off and reviewWitnessed administration. Annual competency reassessment. 24/7 haemophilia nurse helpline contact provided.
Physiotherapy & Joint Care
🏊 Recommended Physical Activities
- Swimming — excellent low-impact, builds muscle
- Cycling — knee-protective, cardiovascular fitness
- Walking, yoga, pilates
- Golf, fishing, bowling
- Controlled gym weights — with physiotherapy guidance
- Contact sports (rugby, boxing, martial arts) — AVOID
- Football (soccer) — high risk in severe haemophilia
🦿 Joint Assessment & Rehabilitation
- Target joint: >3 bleeds in 6 months — intensive physiotherapy + consider prophylaxis intensification
- Haemophilia Joint Health Score (HJHS) — annual assessment
- Ultrasound joint imaging — synovitis detection
- Radiosynovectomy for chronic synovitis (radioisotope injection)
- Orthopaedic surgery (joint replacement) under full factor cover
- Weight management crucial — reduces joint loading
Inhibitor Management — Immune Tolerance Induction (ITI)
Immune Tolerance Induction (ITI): High-dose factor FVIII given daily (50–200 IU/kg/day) for 12–24 months to desensitise immune system and eradicate inhibitors. Success rate ~70% in good prognosis patients.
Good prognosis factorsPeak inhibitor <200 BU, starting titre <10 BU
High-dose ITI200 IU/kg/day (Bonn protocol)
Low-dose ITI50 IU/kg 3x/week (Malmö low-dose)
DurationUntil inhibitor <0.6 BU and FVIII recovery normalises
MonitoringMonthly Bethesda assay + FVIII recovery
GCC formulary challenge: ITI is extremely expensive — high factor usage for 1–2 years. Access varies across GCC countries. KFSH Riyadh and Hamad Medical Centre Doha have established ITI programmes.
- Central venous access essential for ITI
- Bypass therapy (rFVIIa/aPCC) for breakthrough bleeds during ITI
- Emicizumab as concurrent prophylaxis during ITI — reduces bleed burden
Surgical Planning
| Phase | Action | Target |
| Pre-operative (1 week) | Factor level, inhibitor screen, FBC, coag screen, G&S | Baseline established |
| Pre-operative (day of) | Factor infusion 30–60 min pre-op | 100% factor level |
| Intra-operative | Continuous factor infusion or bolus q4–6h; anaesthetic team aware | Maintain >80% |
| Post-operative day 1–3 | Factor q8–12h; surgical site monitoring; drain output | 50–80% |
| Post-operative day 4–14 | Factor q12–24h; physiotherapy starts; wound assessment | 30–50% |
| After day 14 | Return to standard prophylaxis regimen | Trough >1% |
Emergency Preparedness & Travel
🆘 Emergency Card & Alert Bracelet
- Every patient must carry a haemophilia emergency card (in Arabic and English)
- Card includes: diagnosis, severity, factor product, inhibitor status, haemophilia centre contact
- Medical alert bracelet/necklace — worn at all times
- Emergency contacts: haemophilia nurse specialist, on-call haematologist
- WFH (World Federation of Hemophilia) global treatment directory
✈️ Travel with Factor Concentrates
- Obtain doctor's letter on hospital letterhead (Arabic + English)
- Factor must be in original packaging with pharmacy label
- Cold chain: insulated bag with ice packs for travel; factor stored 2–8°C
- Carry at least 3–5 days extra supply above planned need
- WFH treatment centre directory for destination country
- Inform airline in advance — sharps/needles in cabin baggage
- Travel insurance: disclose haemophilia, ensure emergency treatment covered
Adolescent Transition to Adult Services
- Transition planning begins at age 14–16
- Young person takes increasing ownership of self-management
- Education: independence with home therapy, vein care
- Vocational guidance: careers compatible with haemophilia
- Sexual health: passing on the gene — genetics counselling
- Mental health screening: anxiety/depression common in chronic disease
- Substance misuse risk — illicit drug IV use destroys veins
- Transition clinic: joint paediatric/adult haematology appointment
- Youth ambassador programmes (WFH/national societies)
- HCV/HIV testing if diagnosed before 1992 (contaminated products era)
GCC Haemophilia Context
🧬 Consanguinity & Genetic Prevalence
Consanguineous marriage (first-cousin marriage) rates in GCC: Saudi Arabia ~30–40%, UAE ~25–30%, Qatar ~35–40% — significantly higher than global averages. This elevates prevalence of autosomal recessive conditions and increases carrier frequency.
- Haemophilia A & B: X-linked — consanguinity does not directly increase frequency but increases chance of carrier mothers having affected children
- vWD type 3: autosomal recessive — significantly more common in GCC due to consanguinity
- Glanzmann's thrombasthenia: particularly prevalent in Jordanian and Arab populations — autosomal recessive
- Bernard-Soulier syndrome: elevated frequency in consanguineous families
- Carrier testing essential for sisters/daughters of haemophilia patients
- Factor VIII/IX gene mutation analysis available in GCC reference labs
- Preimplantation Genetic Testing (PGT) available in select GCC centres for haemophilia
- Premarital genetic screening programmes: Saudi Arabia, UAE, Qatar — mandatory for some conditions, voluntary for others
National Haemophilia Registries & Centres
Haemophilia Centres (GCC)
Saudi ArabiaKFSH&RC Riyadh; King Abdullah Medical City, Makkah; King Fahad Hospital
QatarHamad Medical Corporation, Doha (National Haemophilia Centre)
UAESheikh Khalifa Medical City Abu Dhabi; Tawam Hospital Al Ain
KuwaitKuwait Cancer Control Centre Haemophilia Unit
BahrainSalmaniya Medical Complex
OmanRoyal Hospital Muscat
Haemophilia Societies & Registries
- Saudi Haemophilia Society (SHS) — national registry, patient support, annual conference
- Emirates Haemophilia Society (EHS) — UAE registry, awareness campaigns
- Qatar Haemophilia Society
- WFH (World Federation of Hemophilia) — global registry, treatment support
- WFH treatment fund provides factor to lower-resource settings in region
Neonatal Diagnosis
- Family history of haemophilia → plan delivery at haemophilia centre or with haematology support
- Cord blood sampling at birth: FVIII and FIX levels
- FIX levels physiologically low at birth — may need repeat at 6 months
- Vitamin K given at birth (IM route acceptable with precaution in at-risk neonates)
- AVOID vacuum extraction, forceps delivery, fetal scalp electrodes in suspected haemophilia
- Circumcision should NOT be performed until haemophilia excluded — cultural sensitivity required when discussing with families
- Neonatal ICH can occur — neonatal team alert essential
- Head ultrasound at birth for at-risk neonates
- Carrier mothers: FVIII/vWF levels often halved during pregnancy — advise on peripartum management
- Carrier diagnosis: female relatives should be tested proactively
Girls & Women with Bleeding Disorders
Often under-diagnosed: vWD affects both sexes equally. Carrier females may have FVIII levels 30–70% — symptomatic. Heavy menstrual bleeding (HMB) is the commonest presentation in females.
- vWD: commonest bleeding disorder in women — accounts for majority of unexplained HMB
- Haemophilia carrier females: mean FVIII ~50% — can have levels <40% (symptomatic)
- Screen with FVIII/FIX level + vWF antigen + vWF activity (Ristocetin cofactor)
- Treatment: DDAVP, tranexamic acid, hormonal therapy (combined OCP/Mirena)
- Obstetric risks: postpartum haemorrhage (PPH) risk elevated
- Epidural/spinal anaesthesia: safe if FVIII/FIX >50%
- Genetics counselling: 50% chance of passing haemophilia gene to sons (affected) or daughters (carriers)
- GCC cultural context: disclosure to husband/family of carrier status can be psychologically complex — support from haemophilia nurse/counsellor essential
Religious & Cultural Considerations
🌙 Ramadan & Factor Administration
- Oral medications (tranexamic acid) can be taken at suhoor/iftar
- Subcutaneous injections (emicizumab, DDAVP SC) are permissible during fasting by most Islamic scholars (injection ≠ eating)
- IV infusions: fatwa varies — most scholars permit for medical necessity
- Prophylaxis schedule adjustment: switch to EOD or fortnightly EHL products to reduce infusion burden
- Discuss Ramadan plan with patient and haematologist in advance
- Fluid restriction around DDAVP doses — be mindful of fasting state (hyponatraemia risk higher)
🕋 Hajj & Haemophilia
- Advance planning at least 3 months before Hajj/Umrah season
- Calculate factor requirements for 2–4 weeks + emergency supply
- Liaise with Hajj Ministry Medical Mission for factor storage at Mina camps
- Haemophilia Saudi Society: register patients for Hajj medical support
- Cold storage for factor at Hajj accommodations — liaise with hotel/camp
- Emicizumab (monthly dosing) ideal for Hajj period — single dose before departure
- Emergency haemophilia care available at Noor Specialist Hospital and King Abdullah Medical City, Makkah
🕌 Halal Factor Concentrates
Halal compliance: Some plasma-derived factor concentrates use porcine (pig-derived) gelatin as a stabiliser. Recombinant products are generally free of animal-derived components and are preferred as halal-compliant.
- Recombinant FVIII (Advate, Kogenate, Nuwiq): no animal-derived stabilisers — halal-compliant
- Recombinant FIX (BeneFIX, Rixubis): halal-compliant
- Emicizumab: synthetic bispecific antibody — halal-compliant
- Plasma-derived concentrates: check product PI for excipients (gelatin content)
- Islamic Fiqh Council: in cases of necessity (darura), non-halal medicines are permitted if no halal equivalent available and life is at risk
- Document patient's preference in care plan
- GCC formularies increasingly stocking recombinant products as first line
- Discuss with patient and family — religious scholars may provide individual guidance
GCC Haemophilia Nursing Guide | For educational purposes — always refer to local formulary and haematology guidelines | April 2026