Genetics, Genomics & Inherited Conditions

GCC Nursing Comprehensive Guide — DHA • DOH • SCFHS • QCHP Examination Preparation

Fundamentals GCC Context Clinical Conditions Cancer Genetics Nursing Practice

Genetics Fundamentals

Chromosomes, Genes & DNA — Nursing Basics

Key Vocabulary

  • DNA: Double helix; 4 bases (A-T, G-C). Codes for proteins.
  • Gene: Segment of DNA encoding a functional product.
  • Chromosome: Condensed DNA + protein. Humans have 46 (23 pairs).
  • Autosome: Chromosomes 1–22 (non-sex).
  • Sex chromosomes: XX (female), XY (male).
  • Allele: Alternate form of a gene at a locus.
  • Genotype: Genetic make-up (e.g., Aa).
  • Phenotype: Observable trait/disease expression.
  • Homozygous: Two identical alleles (AA or aa).
  • Heterozygous: Two different alleles (Aa) — often a carrier.

Central Dogma

DNA → RNA (transcription) → Protein (translation)

Mutation Types

  • Point mutation: Single base change (e.g., sickle cell — Glu→Val)
  • Deletion/Insertion: Frameshift changes reading frame
  • Trinucleotide repeat: Expansion disorders (Huntington's, Fragile X)
  • Chromosomal: Deletions, duplications, translocations, aneuploidy
De Novo Mutations: New mutation not present in either parent. Important because negative family history does NOT rule out genetic disease. Examples: achondroplasia (85% de novo FGFR3), some BRCA variants, Turner syndrome.

Inheritance Patterns

PatternKey FeaturesRecurrence RiskExamples
Autosomal DominantAffected in every generation; male & female equally; one affected parent usually present50% each child if one parent affectedHuntington's, Marfan, BRCA1/2 (dominantly inherited susceptibility), achondroplasia, neurofibromatosis
Autosomal RecessiveBoth parents usually unaffected carriers; consanguinity raises risk; skips generations25% affected; 50% carrier; 25% unaffectedSickle cell, thalassaemia, cystic fibrosis, PKU, G6PD, Gaucher
X-linked DominantFemales & males affected; no male-to-male transmission; affected father → all daughters affected50% (mother carrier)Fragile X (technically complex), MECP2 duplication, Rett syndrome
X-linked RecessiveMainly affects males; carrier females usually unaffected; no male-to-male transmission; maternal inheritance50% of sons affected; 50% of daughters carriersHaemophilia A/B, Duchenne MD, G6PD deficiency, colour blindness
MitochondrialMaternal inheritance only; affects both sexes but passed only via mother; variable expression (heteroplasmy)Variable — all children of affected mother at riskMELAS, Leber's optic neuropathy, MERRF
Penetrance vs Expressivity: Penetrance = proportion of people with the genotype who show any phenotype (e.g., BRCA1 has ~70% lifetime breast cancer penetrance). Expressivity = degree to which phenotype is expressed among those who show it (e.g., neurofibromatosis varies from a few spots to severe disease). Reduced penetrance can make a condition appear to "skip" generations mimicking recessive inheritance.

Pedigree Drawing Conventions

Standard Symbols

  • Circle = female; Square = male; Diamond = unknown sex
  • Filled shape = affected; half-filled = carrier (AR)
  • Horizontal line = mating; double horizontal line = consanguineous mating
  • Vertical line descending = offspring
  • Diagonal line through shape = deceased
  • Arrow = proband (index case presenting for care)
  • Dashed outline = obligate carrier
  • Generations numbered with Roman numerals (I, II, III)
  • Individuals numbered left to right within generation

Reading a Pedigree — Exam Tips

  • Every generation affected → think AD
  • Only males affected, carried through females → think X-linked recessive
  • Unaffected parents, affected child → think AR
  • Only through maternal line → think Mitochondrial
  • Double line between parents → consanguinity → raises AR risk
  • Single affected child, unaffected parents with no family history → consider de novo

Chromosomal Disorders

Trisomy 21 (Down Syndrome)

1:700 births
  • Extra chromosome 21
  • Features: hypotonia, epicanthal folds, Brushfield spots, simian crease, AV septal defect
  • Risk rises sharply with maternal age >35
  • Screening: nuchal translucency + PAPP-A + hCG (T1 combined test)
  • Dx: karyotype, NIPT, amniocentesis

Trisomy 18 (Edwards) & 13 (Patau)

Often lethal
  • T18: Clenched fists, rocker-bottom feet, micrognathia, VSD; 90% die <1yr
  • T13: Holoprosencephaly, midline facial defects, polydactyly; 80% die <1yr
  • Both: severe intellectual disability in survivors
  • Counselling: comfort care vs intervention discussion

Sex Chromosome Disorders

  • Turner (45,X): Short stature, webbed neck, ovarian dysgenesis, coarctation of aorta, infertility; manage with GH + oestrogen
  • Klinefelter (47,XXY): Tall, small testes, infertility, gynaecomastia, testosterone deficiency; testosterone replacement therapy
  • Both: increased risk of specific cancers

Genetic Testing Methods

TestWhat It DetectsClinical Use
KaryotypeChromosomal number and large structural changesDown/Turner/Klinefelter; recurrent miscarriage; infertility
FISH (Fluorescence In Situ Hybridisation)Specific chromosomal deletions/duplications at targeted loci22q11.2 deletion (DiGeorge); rapid aneuploidy (prenatal)
Chromosomal Microarray (CMA)Sub-microscopic copy number variants (CNVs) genome-wideDevelopmental delay/autism/dysmorphic features with normal karyotype
Sanger SequencingSingle gene mutation confirmationKnown familial variant confirmation; targeted testing
NGS / Gene PanelMultiple genes simultaneously for point mutations & small indelsHereditary cancer panels (BRCA1/2 + others); cardiomyopathy panels
Whole Exome/Genome (WES/WGS)All coding sequences (exome) or entire genomeUndiagnosed rare disease; research
NIPT (cfDNA)Fetal chromosomal aneuploidy from maternal bloodPrenatal screening T21/T18/T13; high sensitivity; confirmatory karyotype needed

Consanguinity & GCC Context

Consanguinity — Definition & Genetics

Coefficient of Relationship (r)

  • First cousins: r = 1/8 → coefficient of inbreeding F = 1/16 (6.25%)
  • First cousins once removed: F = 1/32
  • Second cousins: F = 1/64
  • Uncle–niece or aunt–nephew: F = 1/8
Key Principle: Consanguinity does NOT create new mutations — it increases the probability that both parents carry the SAME recessive allele inherited from a common ancestor, thus dramatically raising the risk of autosomal recessive disease in offspring.

Risk Calculation

For a general AR condition with population carrier frequency q:

Non-consanguineous couple: Risk of AR child = q² (Hardy-Weinberg)

First-cousin couple: Risk = q² + Fq(1-q) ≈ substantially elevated when q is small

For rare conditions, consanguinity can increase risk 5–10 fold over background.

GCC Consanguinity Rates

  • UAE: ~40–50% of marriages consanguineous
  • Saudi Arabia: ~50–60%
  • Qatar: ~45–55%
  • Kuwait: ~40–50%
  • Global average: ~10–15%

Common Autosomal Recessive Conditions in GCC

ConditionGene/LocusGCC PrevalenceKey Feature
Sickle Cell DiseaseHBB (Glu6Val)Carrier rate up to 25% in some Gulf populationsHaemolytic anaemia, vaso-occlusive crises, organ damage
Beta-ThalassaemiaHBB mutationsCarrier 3–9% across GCC; higher in Eastern Province (Saudi)Transfusion-dependent severe anaemia; iron overload
G6PD DeficiencyG6PD (X-linked)5–25% males in GCC countriesHaemolytic anaemia triggered by oxidants, neonatal jaundice
PKU (Phenylketonuria)PAH1:4,000–1:10,000; elevated in consanguineous populationsIntellectual disability if untreated; low-phe diet essential
Familial Mediterranean FeverMEFVHigher in Arabs, Turks, Armenians; common in GCCRecurrent fever, serositis, peritonitis; colchicine treatment
Gaucher DiseaseGBAElevated in Ashkenazi & Arab populationsHepatosplenomegaly, bone pain, pancytopaenia; enzyme replacement
Congenital DeafnessGJB2 (Connexin 26) + others~50% of congenital deafness in GCC is genetic/ARSensorineural hearing loss; newborn screening essential
Congenital HypothyroidismMultiple genesHigher rate in GCC vs Western countriesIntellectual disability if untreated; part of newborn screening

Premarital Genetic Screening Programmes — GCC

UAE

Mandatory since 2010
  • Required before marriage registration
  • Tests: sickle cell, thalassaemia, G6PD, hepatitis B/C, HIV
  • Managed by HAAD (Abu Dhabi) / DHA (Dubai)
  • Genetic counselling provided if results positive
  • Results shared with both parties; marriage not legally prohibited

Saudi Arabia

Mandatory since 2004
  • National Premarital Screening Programme
  • Tests: sickle cell, thalassaemia, hepatitis B/C, HIV
  • Both parties informed of results
  • Compatible couples proceed; incompatible couples counselled
  • Managed through Ministry of Health centres

Qatar

Mandatory (NHSC)
  • National Health Screening Centre
  • Haemoglobinopathy screening for all nationals
  • Part of broader premarital health assessment
  • Genetic counselling integrated into service
  • Expanding to include expanded carrier panel
Nursing Role in Premarital Screening: Explain the purpose of testing (not to prevent marriage but to allow informed decision-making). Maintain confidentiality. Provide non-directive counselling — couples have the right to proceed with marriage even if both carry the same gene. Document consent. Refer to clinical genetics if results are complex. Provide written information in Arabic where possible.

Genetic Counselling Principles

Core Principles (NSGC Framework)

  • Non-directive: Counsellor presents information; patient/family makes own decisions
  • Autonomy: Respect patient's right to choose (including to not know)
  • Beneficence: Act in the patient's best interest
  • Non-maleficence: Avoid harm from disclosure or testing
  • Justice: Equal access to genetic services
  • Confidentiality: Results are private; complex tension with duty to warn relatives

Carrier Screening

Carrier screening identifies individuals who carry one copy of an AR gene variant. Carriers are unaffected but can pass the variant to offspring. When both parents are carriers, each pregnancy has a 25% chance of the condition.

Cascade Screening

After identifying an index case, systematic testing of biological relatives to find other carriers or affected individuals. Most cost-effective approach for conditions like familial hypercholesterolaemia, BRCA mutations, and hereditary haemoglobinopathies.

Common Genetic Conditions in GCC

TypeGenotypeClinical SeverityManagement
Alpha Thal Trait-α/ααSilent carrier; normal CBCGenetic counselling
Alpha Thal Minor--/αα or -α/-αMild microcytic anaemia; often misdiagnosed as iron-deficiencyReassurance; avoid iron supplementation
HbH Disease--/-α (3 gene deletion)Moderate haemolytic anaemia; splenomegaly; Hb 7–10 g/dLFolic acid; monitor; occasional transfusion; avoid oxidants
Hb Barts (Hydrops Fetalis)--/-- (4 gene deletion)Incompatible with life (stillbirth/neonatal death); Hb Barts γ4Intrauterine transfusion in some centres; usually fatal
Beta Thal Minor (Trait)β/β⁺ or β/β⁰Mild anaemia; microcytosis; elevated HbA2 >3.5% (key diagnostic marker)Genetic counselling; iron only if deficient
Beta Thal Intermediaβ⁺/β⁺Non-transfusion-dependent; Hb 7–10; splenomegaly; bone changesHydroxyurea; folic acid; chelation if iron-loaded; HSCT option
Beta Thal Major (Cooley's)β⁰/β⁰Transfusion-dependent; severe anaemia; iron overload; facial changesRegular transfusions (target pre-Hb >9.5); iron chelation; HSCT curative
HbE/Beta ThalHbE + β mutationVariable; mild to thal major severity; common in South/Southeast Asia; seen in GCCDepends on severity; as per thal intermedia/major
Iron Chelation Agents: Desferrioxamine (IV/SC — subcutaneous infusion overnight); Deferasirox (Exjade — oral, once daily); Deferiprone (oral, 3x daily — may cause agranulocytosis, check WBC). Target serum ferritin <1,000 ng/mL.

Sickle Cell Disease Management in GCC

Pathophysiology

Point mutation in HBB gene (Glu→Val at position 6). HbS polymerises under low O₂, causing RBC sickling → haemolysis + vascular occlusion.

GCC-Specific Notes

  • Arabian haplotype (Saudi/Indian corridor) associated with higher HbF — milder course than African haplotype
  • High carrier rates in Eastern Saudi Arabia, Bahrain, Oman
  • Mandatory neonatal screening in UAE and Saudi Arabia

Vaso-Occlusive Crisis (VOC)

  • Trigger: infection, dehydration, cold, stress, hypoxia
  • Pain management: paracetamol → NSAIDs → opioids (WHO ladder)
  • IV fluids (hydration key)
  • Oxygen if SpO₂ <95%
  • Warmth; incentive spirometry

Acute Chest Syndrome (ACS)

EMERGENCY — ACS: New infiltrate on CXR + fever/respiratory symptoms. Most common cause of death in SCD adults. Treat: O₂, incentive spirometry, exchange transfusion, bronchodilators, antibiotics. Avoid fluid overload.

Stroke Prevention

  • TCD (transcranial Doppler) screening from age 2 annually
  • Elevated TCD velocity (>200 cm/s): chronic transfusion programme
  • Hydroxyurea: increases HbF, reduces crises by ~50%

Long-term Complications

  • Avascular necrosis (hip/shoulder)
  • Retinopathy — annual ophthal
  • Nephropathy — ACE inhibitor
  • Priapism — urological emergency
  • Pulmonary hypertension

Drugs to AVOID in G6PD Deficiency

HIGH RISK — Avoid:
  • Primaquine (antimalarial — key exam answer)
  • Dapsone (leprosy/PCP prophylaxis)
  • Rasburicase (uric acid reduction)
  • Nitrofurantoin (UTI antibiotic)
  • Methylene blue (paradoxically causes haemolysis in G6PD)
  • Pegloticase
USE WITH CAUTION:
  • Chloroquine (at higher doses)
  • Quinine (high doses)
  • Aspirin (high doses >1g/day)
  • Vitamin K analogues (menadione)
  • Nalidixic acid

Non-Drug Triggers

  • Fava beans (broad beans) — classic GCC/Mediterranean trigger
  • Severe infections (most common trigger overall)
  • Diabetic ketoacidosis
  • Henna (in severe G6PD variants)

Neonatal G6PD Jaundice

  • G6PD is part of GCC newborn screening
  • Can cause severe neonatal jaundice and kernicterus
  • Mother's diet (fava beans) and drugs passed in breast milk
  • Phototherapy; exchange transfusion if severe
  • Educate family on lifelong trigger avoidance

X-linked Inheritance Note

Hemizygous males most severely affected. Carrier females usually mildly affected but can have haemolysis if lyonisation is unfavourable.

Familial Hypercholesterolaemia (FH)

Genetics

  • Autosomal dominant — LDLR (most common), APOB, PCSK9 mutations
  • Heterozygous FH: 1:200–500; LDL 5–13 mmol/L
  • Homozygous FH: 1:300,000–1,000,000; LDL >13 mmol/L; CAD before age 20

Dutch Lipid Clinic Score

CriterionPoints
Family history: 1st degree with premature CVD or FH1–2
Clinical history: personal premature CAD2
Tendon xanthomata or corneal arcus <45yr4–6
LDL-C 4–4.9 mmol/L1
LDL-C ≥8.5 mmol/L8
DNA mutation confirmed8

Score ≥8 = definite FH; 6–7 = probable; 3–5 = possible

Management

  • High-intensity statin + ezetimibe first-line
  • PCSK9 inhibitors (evolocumab/alirocumab) if LDL target not reached
  • LDL apheresis for homozygous FH
  • Lomitapide/inclisiran — newer agents
  • Target: >50% LDL reduction from baseline; LDL <1.8 mmol/L if high-risk CVD

Cascade Screening

Once a proband is identified, screen all first-degree relatives. Childhood screening from age 5–10 if parent has FH. Cost-effective and potentially life-saving as untreated HeFH carries 20× increased CAD risk.

Cancer Genetics

NICE NG151 Criteria — Offer BRCA Testing If:

  • Personal history of breast cancer + ANY of: diagnosed ≤40 years; bilateral breast cancer; triple-negative breast cancer ≤60yr; Jewish ancestry
  • Ovarian/fallopian tube/primary peritoneal cancer at any age
  • Male breast cancer
  • Family history score: Manchester or equivalent scoring ≥15% BRCA probability
  • Known family BRCA mutation — offer predictive testing
  • Pancreatic cancer + 1 close relative with breast/ovarian/pancreatic cancer

BRCA1 vs BRCA2 Cancer Risks (Lifetime)

CancerBRCA1BRCA2
Female breast cancer~70%~70%
Ovarian cancer~44%~17%
Male breast cancer~1–2%~6–8%
Pancreatic cancerSlight increase~5%
Prostate cancerSlight increase~20% (aggressive)
Risk-Reducing Options for BRCA Carriers: Enhanced surveillance (annual MRI from age 25–30; mammogram from 30–40); Risk-reducing mastectomy (~95% risk reduction); Risk-reducing bilateral salpingo-oophorectomy (>90% ovarian cancer risk reduction — recommended by 35–40 for BRCA1, 40–45 for BRCA2); Chemoprevention (tamoxifen/raloxifene/anastrozole).

Lynch Syndrome (Hereditary Non-Polyposis Colorectal Cancer)

Genetics

  • Autosomal dominant — MLH1, MSH2, MSH6, PMS2 (MMR genes)
  • EPCAM gene deletions also cause Lynch
  • Loss of MMR function → microsatellite instability (MSI)
  • CRC risk: 40–70% lifetime (MLH1/MSH2 highest)
  • Endometrial cancer: 40–60% (MLH1/MSH2)
  • Also: ovarian, gastric, urinary tract, small bowel, brain (Turcot variant)

Amsterdam Criteria II

3–2–1 rule: ≥3 relatives with Lynch-associated cancer (one = first-degree relative of the other two); ≥2 successive generations; ≥1 case diagnosed <50 years; FAP excluded; tumours verified by pathology.

Universal Tumour Testing

All colorectal and endometrial cancers should undergo reflex MSI/IHC testing for MMR proteins. Loss of a specific MMR protein on IHC directs germline testing:

  • Loss of MLH1/PMS2: BRAF V600E / MLH1 promoter methylation first (somatic); if negative → germline MLH1 testing
  • Loss of MSH2/MSH6: directly to germline MSH2/MSH6/EPCAM

Surveillance

  • Colonoscopy every 1–2 years from age 25 (or 2–5yr before youngest affected relative)
  • Endometrial sampling/TVU annually from age 35 (consider RRSO after childbearing)
  • Aspirin 600mg/day reduces CRC risk in Lynch (CAPP2 trial)

Familial Adenomatous Polyposis (FAP)

Genetics

  • Autosomal dominant — APC gene (chromosome 5q22)
  • Hundreds to thousands of colorectal polyps developing in teens/20s
  • Near 100% risk of CRC by age 40 if untreated
  • Attenuated FAP (AFAP): fewer polyps (<100), later onset
  • MUTYH-associated polyposis (MAP): autosomal recessive; biallelic MUTYH mutations

Extracolonic Manifestations

  • Duodenal/ampullary adenomas (Spigelman classification)
  • Desmoid tumours (more common if APC mutation codon 1310–2000)
  • Osteomas (jaw); epidermoid cysts; CHRPE (congenital hypertrophy of RPE)
  • Gardner syndrome (FAP + soft tissue tumours)
  • Turcot syndrome (FAP + medulloblastoma)

Management

  • Annual flexible sigmoidoscopy/colonoscopy from age 12–14
  • Prophylactic colectomy recommended by late teens/early 20s (or when polyps >20 or high-grade dysplasia)
  • Options: proctocolectomy + IPAA (ileal pouch) or subtotal colectomy + IRA
  • Upper GI endoscopy every 1–5 years (Spigelman stage-dependent)

Li-Fraumeni Syndrome & Pre/Post-Test Counselling

Li-Fraumeni Syndrome

  • Autosomal dominant — TP53 gene ("guardian of the genome")
  • Childhood-onset sarcomas, adrenocortical carcinoma, brain tumours, breast cancer <30yr, leukaemia
  • ~90% lifetime cancer risk
  • Whole-body MRI annually (Toronto Protocol)
  • Avoid radiation-based imaging/treatment where possible
  • Consider testing all close relatives if confirmed

Genetic Counselling: Pre & Post-Test

Pre-Test Counselling Must Include:
  • Purpose, nature and limitations of the test
  • Possible results (positive / negative / variant of uncertain significance — VUS)
  • Implications for patient and relatives
  • Emotional/psychological impact
  • Insurance and employment implications (discuss with patient)
  • Right to decline testing (autonomy)
  • Written information provided
Post-Test Counselling: Explain results in plain language. Provide written summary. Discuss surveillance/management options. Offer referral to clinical psychology. Address duty to warn family members — this is an ethical tension (see Tab 5).

Genomic Nursing Practice

Taking a Three-Generation Family History

Structure

  1. Start with the proband (patient)
  2. Ask about parents, siblings, children (first-degree relatives)
  3. Ask about grandparents, aunts/uncles, cousins (second/third degree)
  4. Record: age, health status, cause of death, age at diagnosis
  5. Ask specifically about: cancer, heart disease, blood disorders, learning disability, miscarriages, stillbirths, birth defects, consanguinity, ethnicity
  6. Update at each visit — family history is dynamic

Tool

Use standard pedigree notation (see Tab 1). Document in medical record. Flag to genetics team if red flags present.

Red Flags Requiring Genetics Referral

  • Cancer diagnosed at unusually young age (<50yr)
  • Multiple primary cancers in one individual
  • Bilateral cancers (both breasts, both kidneys)
  • Rare tumour type (adrenocortical carcinoma, male breast cancer)
  • Multiple affected family members with same or related cancers
  • Multiple congenital abnormalities in a child
  • Unexplained intellectual disability + dysmorphic features
  • Consanguineous parents + sick child
  • Recurrent pregnancy loss ≥3
  • Ethnic background with high-frequency recessive conditions

Informed Consent for Genetic Testing

Genetic testing requires enhanced consent beyond standard clinical consent due to the following unique features:

Unique Features of Genetic Information

  • Results have implications for blood relatives (not just patient)
  • Reveals permanent, immutable information about self
  • May reveal unexpected findings (misattributed paternity, unsuspected conditions)
  • Variants of Uncertain Significance (VUS) create ambiguity
  • Insurance/employment risk in some jurisdictions
  • Psychological impact can be significant

Consent Documentation Must Include

  • Nature of the test and what it can/cannot detect
  • Who will have access to results
  • How results will be communicated
  • Right to withdraw consent before analysis
  • Storage and future use of DNA/samples
  • Incidental findings policy — does the lab report unexpected findings?
Right NOT to know: Patients have the right to decline knowing their genetic test results or decline testing altogether. This must be respected even if results would benefit the patient clinically.

Duty to Warn Relatives — Ethical Tensions

The Ethical Conflict

When a patient carries a pathogenic variant (e.g., BRCA1, Lynch syndrome, Huntington's), close relatives may be at 50% risk. Should the nurse/genetics team breach confidentiality to warn them?

Competing Principles:
  • Confidentiality (patient): Patient may refuse to tell relatives
  • Beneficence (relatives): Relatives could benefit from testing and surveillance
  • Autonomy (relatives): Relatives have a right to know/right not to know

Professional Guidance (UK/International)

Recommended approach:
  1. Explore reasons for non-disclosure with patient
  2. Discuss benefits of family communication; offer to write letters for patient to share
  3. Document discussions clearly
  4. Seek ethics committee/clinical genetics input if patient refuses and relatives face serious harm
  5. In GCC context: family-centred culture may support disclosure but patient consent still paramount
  6. Breach of confidentiality justified ONLY if: serious harm is imminent, disclosure limited to minimum necessary, and all other means exhausted

Pharmacogenomics — CYP450 Polymorphisms

CYP2D6 — Codeine / Opioid Metabolism

Metaboliser TypeCYP2D6 ActivityClinical Effect with Codeine
Poor Metaboliser (PM)NoneNo conversion to morphine — no analgesia
Intermediate Metaboliser (IM)ReducedReduced effect
Normal/Extensive (EM)NormalStandard effect
Ultra-Rapid Metaboliser (UM)Very highTOXIC morphine levels — respiratory depression, death
EXAM ALERT: CYP2D6 ultra-rapid metabolisers given codeine (including via breast milk) can develop fatal morphine toxicity. MHRA/FDA contraindicated codeine in breastfeeding mothers and children <12 yr due to this risk.

Other Key CYP Polymorphisms

  • CYP2C19: Clopidogrel activation — PMs have reduced platelet inhibition (increased stent thrombosis risk); PPIs metabolism
  • CYP2C9 + VKORC1: Warfarin dosing — variants affect sensitivity; responsible for many warfarin-related bleeds
  • TPMT: Azathioprine/6-MP metabolism — TPMT deficiency → severe myelosuppression; test before prescribing
  • HLA-B*57:01: Abacavir hypersensitivity — screen all HIV patients before starting abacavir
  • HLA-B*58:01: Allopurinol severe cutaneous adverse reactions — more common in Asian/GCC populations; consider testing
  • G6PD: Primaquine/rasburicase — haemolysis (see Tab 3)

UK Newborn Bloodspot (Guthrie) — 9 Conditions

  • Congenital hypothyroidism (TSH)
  • Phenylketonuria — PKU (phenylalanine)
  • Cystic Fibrosis (IRT/CFTR)
  • Sickle cell disease (HPLC)
  • Medium-chain acyl-CoA dehydrogenase deficiency (MCADD)
  • Maple syrup urine disease (MSUD)
  • Isovaleric acidaemia (IVA)
  • Glutaric aciduria type 1 (GA1)
  • Homocystinuria (HCU)

Taken at day 5 of life (day 5–8). Heel prick onto filter paper card.

GCC Newborn Screening Expansions

  • UAE/Saudi/Qatar: expanded panels typically include 20–50 conditions
  • G6PD — mandatory in UAE, Oman, Saudi; critical in GCC due to high prevalence
  • Congenital adrenal hyperplasia (17-OHP)
  • Biotinidase deficiency
  • Galactosaemia
  • Amino acid disorders (tandem MS)
  • Fatty acid oxidation disorders
  • Hearing screen (OAE/AABR) — separate but same newborn period
Nursing Role: Explain purpose/procedure to parents. Obtain consent. Correct timing (day 5). Label accurately. Ensure follow-up if screen positive. Positive screen = recall for diagnostic testing, not diagnosis itself.

GCC Exam Prep — MCQ Practice

Practice questions aligned with DHA, DOH, SCFHS, and QCHP examination style. Click "Show Answer" to reveal the explanation.

Interactive: Inheritance Pattern Identifier

Select the features observed in the pedigree:

Genetics MCQ Bank

1. A 28-year-old Emirati woman is found to be a carrier of the HBB sickle cell mutation during premarital screening. Her partner is also found to be a carrier. What is the probability that their first child will have sickle cell disease?
A. 100%
B. 75%
C. 50%
D. 25%
Correct: D — 25%
When both parents are carriers (Aa × Aa), the offspring probability is: 25% AA (unaffected), 50% Aa (carrier), 25% aa (affected). This is classic autosomal recessive inheritance. UAE's mandatory premarital screening exists precisely to identify these couples and provide genetic counselling before marriage.
2. A 3-day-old male neonate in a Dubai hospital develops severe jaundice (bilirubin 380 μmol/L). His mother consumed fava bean stew during the third trimester. The most likely diagnosis is:
A. ABO incompatibility
B. Physiological jaundice
C. G6PD deficiency haemolytic jaundice
D. Biliary atresia
Correct: C — G6PD deficiency haemolytic jaundice
G6PD deficiency is prevalent in GCC (up to 25% of males). Fava beans contain vicine and convicine — oxidants that trigger haemolysis in G6PD-deficient individuals. These can cross the placenta and transfer via breast milk. The severity and timing (day 3) are characteristic of G6PD haemolytic jaundice. Management: phototherapy urgently, exchange transfusion if rising despite phototherapy, avoid oxidant triggers, educate family. Part of UAE/Saudi mandatory newborn screening.
3. A pedigree shows that all affected individuals in three generations are female, and ALL children of an affected mother (both sons and daughters) show the condition. The father of affected individuals is always unaffected. This pattern most strongly suggests:
A. Autosomal dominant inheritance
B. X-linked dominant inheritance
C. Mitochondrial inheritance
D. Autosomal recessive inheritance
Correct: C — Mitochondrial inheritance
Key feature: ALL children of an affected MOTHER are at risk (or affected) regardless of sex, but the condition is NEVER passed by an affected father — this is the hallmark of mitochondrial (maternal) inheritance. Mitochondria are inherited entirely from the oocyte, not from sperm. Examples: MELAS, MERRF, Leber's hereditary optic neuropathy. Note: X-linked dominant also affects daughters of affected fathers — not seen here — making mitochondrial the correct answer.
4. A Saudi nurse is caring for a 14-year-old with beta-thalassaemia major who is on a regular transfusion programme. Her serum ferritin is 3,500 ng/mL. Which nursing intervention is the PRIORITY?
A. Administer iron supplements to correct anaemia
B. Administer iron chelation therapy as prescribed
C. Increase transfusion frequency
D. Prepare for bone marrow biopsy
Correct: B — Iron chelation therapy
In transfusion-dependent thalassaemia, each unit of blood deposits ~200–250mg iron. With no physiological iron excretion mechanism, iron accumulates in the heart, liver, and endocrine organs causing cardiomyopathy, hepatic fibrosis, and endocrinopathy. Target ferritin <1,000 ng/mL. Chelation agents: Desferrioxamine (DFO — SC infusion), Deferasirox (oral), Deferiprone (oral). Iron supplements (option A) are CONTRAINDICATED — they would worsen iron overload. HSCT (not BMBx) is the curative option.
5. A 35-year-old woman with a known BRCA1 pathogenic variant attends for pre-test counselling for her 25-year-old sister. What is the probability that the sister also carries the BRCA1 variant?
A. 100%
B. 75%
C. 50%
D. 25%
Correct: C — 50%
BRCA1/2 mutations follow autosomal dominant inheritance. A parent who carries a BRCA1 mutation will pass it to 50% of their offspring. Siblings share 50% of their genes (first-degree relatives). Therefore, the sister has a 50% prior probability of having inherited the same BRCA1 variant — this is reduced to near certainty (positive) or near zero (negative) once genetic testing is completed. This is the rationale for cascade screening of first-degree relatives.
6. A patient is prescribed codeine 30mg for post-operative pain. 2 hours later, his respiratory rate drops to 8/minute and he becomes difficult to rouse. Which pharmacogenomic explanation is MOST likely?
A. CYP2D6 poor metaboliser — codeine not converted to morphine
B. CYP2D6 ultra-rapid metaboliser — excessive morphine production
C. CYP2C9 poor metaboliser — reduced drug clearance
D. TPMT deficiency — myelosuppression
Correct: B — CYP2D6 ultra-rapid metaboliser
Codeine is a prodrug metabolised by CYP2D6 to morphine. Ultra-rapid metabolisers (1–2% Caucasian, up to 10–29% in some North African/Arabian populations) rapidly convert large amounts of codeine to morphine, causing respiratory depression and potential death. Management: NALOXONE immediately; support ventilation; avoid codeine and tramadol in known UMs. This is a black-box warning: codeine contraindicated in children <12yr and breastfeeding mothers. CYP2D6 UM prevalence is important in GCC nursing practice.
7. In a Qatari family with a child diagnosed with phenylketonuria (PKU), which statement about the inheritance pattern and carrier status is CORRECT?
A. The parents must both be affected with PKU to produce an affected child
B. Both parents are obligate carriers; they each have a 25% chance of an affected child with each pregnancy
C. Only the mother passes PKU to children
D. The condition is X-linked so only males are at risk
Correct: B
PKU (PAH gene mutations) is autosomal recessive. For an affected child to be born, BOTH parents must carry at least one copy of the PKU mutation — making them obligate carriers. Each subsequent pregnancy has a 25% risk of PKU, 50% chance of being a carrier, and 25% chance of being unaffected non-carrier. Consanguinity (common in Qatar) significantly increases the probability of two carriers meeting. Newborn screening allows early dietary intervention (low-phenylalanine diet) preventing intellectual disability.
8. Regarding G6PD deficiency management, which of the following should a nurse instruct the patient to AVOID?
A. Paracetamol and amoxicillin
B. Primaquine, dapsone, nitrofurantoin, and fava beans
C. Metformin and lisinopril
D. Iron supplements and folic acid
Correct: B — Primaquine, dapsone, nitrofurantoin, and fava beans
These are the classic oxidant triggers for G6PD haemolysis. The G6PD enzyme protects RBCs from oxidative damage by generating NADPH. Without functional G6PD, RBCs are vulnerable to oxidants. Primaquine (antimalarial) and dapsone are the most commonly tested drug triggers in licensing exams. Fava beans (ful medames) are culturally significant in the GCC/Arab world — patient education about this dietary trigger is critical. Paracetamol and amoxicillin (option A) are SAFE in G6PD deficiency.
9. Which genetic testing method is MOST appropriate to confirm a suspected diagnosis of DiGeorge syndrome (22q11.2 deletion) in a neonate with conotruncal heart defect and hypocalcaemia?
A. Standard karyotype (G-banding)
B. FISH for 22q11.2 deletion
C. Whole exome sequencing
D. Mitochondrial DNA analysis
Correct: B — FISH for 22q11.2 deletion
DiGeorge/velocardiofacial syndrome is caused by a ~3Mb deletion at 22q11.2. This deletion is too small to be seen on standard karyotype (which has ~5–10Mb resolution). FISH using a probe specific for the 22q11.2 locus detects this deletion rapidly and reliably — it is the first-line test for suspected 22q11.2 deletion syndrome. Note: chromosomal microarray (CMA) would also detect this and is increasingly first-line in many centres. Whole exome sequencing would also eventually find it but is more expensive and time-consuming.
10. A nurse is providing pre-test genetic counselling for a woman considering BRCA1/2 testing. Which statement BEST reflects non-directive counselling?
A. "You should definitely have the test because early detection saves lives."
B. "I'll explain all the possible outcomes and support whatever decision you make."
C. "Since your mother had BRCA1, you must be tested immediately."
D. "If you don't test, you may be putting your children at risk."
Correct: B
Non-directive counselling is a fundamental principle of genetic counselling. The counsellor's role is to provide accurate, balanced information about the test — what it can detect, possible results (positive, negative, VUS), implications for the patient and family, surveillance options, and psychological impact — and then support the patient in making their OWN autonomous decision. Options A, C, and D are all directive — they direct the patient toward a specific action rather than facilitating informed autonomous choice. Respecting the right not to know is equally important.

Quick Reference: Exam High-Yield Points

Must-Know Numbers

  • First cousin inbreeding coefficient: F = 1/16 (6.25%)
  • AR offspring risk (both carriers): 25%
  • AD offspring risk (one parent affected): 50%
  • X-linked recessive: sons of carrier mother at 50% risk
  • BRCA1 lifetime breast cancer risk: ~70%
  • Lynch syndrome CRC risk: 40–70% lifetime
  • HbA2 >3.5% = beta-thalassaemia trait
  • TCD velocity >200 cm/s = chronic transfusion in SCD

Classic GCC Exam Scenarios

  • Consanguineous couple + sick child → think AR condition
  • Fava beans + jaundice/anaemia → G6PD deficiency
  • Ferritin 3,500 in thalassaemia → chelation therapy (NOT iron)
  • Codeine + respiratory depression → CYP2D6 ultra-rapid metaboliser
  • Premarital screen positive for sickle trait → non-directive counselling
  • Newborn jaundice day 2–3 in GCC → check G6PD
  • All children of affected mother affected → mitochondrial
  • Young woman (<40) bilateral breast cancer → offer BRCA testing